VAN GOOR, Frederick
1 entries in the GMN corpus.
2011 CE
#13571
Correction of the 508del-CFTR protein processing defect in vitro by the investigational drug VX-809.
NEGULESCU, Paul A. VAN GOOR, Frederick HADIDA, Sabine GROOTENHUIS, Peter D. J. (1960 – 2019) & et al.
Negulescu and colleagues published a "proof of concept" experiment showing that the novel molecule called VX-809 could correct in vitro the very common and critical 508del-CFTR mutation identified by Collins. (See GM …